A baby was born with a syndrome so rare it doesn’t have a name – after doctors spotted his “beautiful” wide eyes. Oska-Gray ...

International Angelman Day also marks the birthday of Dr. Harry Angelman, the British pediatrician who first identified the ...

Ionis Pharmaceuticals, which is developing a treatment for the rare neurological disease of Angelman syndrome (AS), turned to Lifetime Television’s “Behind the Mystery” series to increase public ...

MIDDLETON, Mass., Nov. 6, 2025 /PRNewswire/ -- MavriX Bio, a clinical-stage biotechnology company focused on the development of transformative genetic therapies for Angelman syndrome (AS), today ...

Take advantage of TipRanks Premium at 50% off! Unlock powerful investing tools, advanced data, and expert analyst insights to help you invest with confidence. Ultragenyx Pharmaceutical ( (RARE)) just ...

On Tuesday, the U.S. Food and Drug Administration (FDA) granted Breakthrough Therapy designation to Ionis Pharmaceuticals Inc.’s (NASDAQ:IONS) ION582 for Angelman syndrome (AS), a rare neurological ...

Researchers from Brain Research Institute, Niigata University, Japan have revealed that environment influences social behaviors in autism. By using zebrafish that have a mutation in ube3a, a gene ...

Company expects to complete Phase 3 Aspire study in the second half of 2026 Aurora study of GTX-102 in additional ages and genotypes on track to initiate in the second half of 2025 “The accelerated ...

CHESHIRE, Conn. (WTNH) — The General Motors charity car show was held on Sunday in Cheshire, benefitting families with children diagnosed with Angelman Syndrome. Quinnipiac students create customized ...

3-year-old Bellamy Bresaw of Bow was diagnosed with Angelman Syndrome at nine months old. Credit: Delores Flanders / Courtesy Delores Flanders and her family are hosting a fundraiser at Boutwell’s ...

Actor Colin Farrell has opened up about the difficult decision to move his son James, who has Angelman syndrome, into a long-term care facility. In an interview this week the actor, 48, revealed he ...

Colin Farrell is elaborating on a big parenting decision he made. The “Penguin” star, 48, revealed in a new interview with Candis magazine that he and his ex, model Kim Bordenave, put their ...