SMA expert Brian Lin, PhD, shares his thoughts on aging with SMA, treatment, advocacy, and supporting patients across their ...

SMA expert Brian Lin, PhD, shares his thoughts on aging with SMA, treatment, advocacy, and supporting patients across their ...

After a meeting with the FDA, Scholar Rock is planning a 2026 resubmission of its application seeking approval of apitegromab ...

Zolgensma outperformed Spinraza in achieving a more sustained clinical response for children with SMA type 1, a comparative ...

Like one of her favorite poems describes, columnist Brianna Albers always feels like she's digging herself out of a new hole in her life.

Combining the experimental and approved SMA therapies BIO101 and Spinraza in the lab was found to improve muscle function in ...

Family caregivers express immense devotion to others, but they should also remember self-care, writes columnist.

Spinraza (nusinersen) may help stabilize lung function in people with SMA types 2 and 3, delaying the need for breathing ...

For columnist Alyssa Silva, control has always been her safety net. But in reality, it doesn't protect her; it exhausts her.

Try these practical tips for travel with SMA, with advice on packing, accessible accommodations, and health management.

A study found mutations that cause SMA may trigger problems with bone cell communication, suggesting a potential new way to treat weak bones.

Columnist Sherry Toh can't fathom generative AI replacing human empathy when it comes to caregiving for people with rare diseases.