Gene therapy is a medical treatment that works by changing or fixing a person's genes to treat or prevent disease ...

Under the agreement, participating states will receive “discounts and rebates” from the drugmakers if the treatments don’t ...

People are often encouraged to “know their status,” however this healthy habit can be applied to more than just safe-sex practices. Although they are not the only community who suffers with sickle ...

Medicaid is doing a novel payment system for the new, promising and expensive sickle cell treatment. It may become a model ...

Sickle cell disease refers to a group of genetic diseases that impact a protein that ferries oxygen through the blood. That protein is called hemoglobin, and in sickle cell disease, aberrant ...

NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in vaso-occlusive crises for eligible patients.

To continue reading this content, please enable JavaScript in your browser settings and refresh this page. Ryan Dodson, 18, was diagnosed with sickle cell disease ...

At the weekend in Kampala, a piece of news landed that could reshape the future of one of the world’s most neglected diseases. The United States Patent and Trademark Office (USPTO) had accepted a ...

Crescent-shaped red blood cells from a sickle cell disease patient in 1972. The disorder affects hemoglobin, the protein in red blood cells that carries oxygen. A genetic mutation causes the cells to ...

Scientists have found a potential new gene variant target to treat sickle cell disease, an inherited blood disorder that affects about 300,000 people globally each year, with limited treatment options ...

A newly opened sickle cell treatment center at the Medical University of South Carolina is facing growing criticism from patients and civil rights advocates who say they are being denied adequate pain ...

Sickle cell patients and their families are speaking out, saying their pain is being treated with a one-size-fits-all approach that fails to recognize how diffe ...